The FDA has approved fitusiran for bleeding management in hemophilia A or B in patients aged 12 years and older, with or without factor VIII or IX inhibitors. Sanofi, which markets fitusiran as Qfitlia, announced the FDA’s approval in a press release.
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The findings coincide with patient reports of experiencing increased vaso-occlusive episodes during menses.
Adrián Mosquera Orgueira, MD, PhD, spoke of his team's study into machine learning tools for improving risk stratification.
The Clinical Practice Guidance document issued by the EHA, ISTH, EAHAD, and ESO addresses both hemophilia A and B.
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